MDA CCN GTx Case Discussion Group

October 22, 2025

MDA CCN GTx Case Discussion Group

Target Audience

This activity is designed for an audience of nurses, nurse practitioners, pharmacists, physicians, physician associates and social workers.

Learning Objectives

  • Ask key questions related to gene transfer therapy and long-term monitoring of patients.
  • Identify ways to collaborate with multidisciplinary care teams to coordinate care within their unique clinic setting.
  • Leverage tools and resources discussed to streamline access and patient outcomes for gene transfer therapy.

Commercial Support
There is no commercial support for this activity.

 

Course summary
Available credit: 
  • 1.00 AANP
  • 1.00 AAPA Category 1 CME
  • 1.00 ACPE Pharmacist
  • 1.00 AMA PRA Category 1 Credit™
  • 1.00 ANCC
  • 1.00 ASWB
  • 1.00 Attendance
Course opens: 
09/12/2025
Course expires: 
10/11/2025
Event starts: 
10/22/2025 - 5:00pm EDT
Event ends: 
10/22/2025 - 6:00pm EDT
Cost:
$0.00
Add to calendar: 
Rating: 
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Live Webinar
United States

Planners and Reviewers

Dorothy Duffy, RPh 
Bernadette Makar, MSN, APRN-BC, NP-C 

Broc Pollinger, MSW, LSW, OSW-C 

All of the relevant financial relationships listed for these individuals have been mitigated.

Disclosures
None of the planners or faculty for this educational activity have relevant financial relationship(s) to disclose with ineligible companies whose primary business is producing, marketing, selling, re-selling, or distributing healthcare products used by or on patients.

It is the policy of AKH Inc. to ensure independence, balance, objectivity, scientific rigor, and integrity in all of its continuing education activities. The author must disclose to the participants any significant relationships with ineligible companies whose products or devices may be mentioned in the activity or with the commercial supporter of this continuing education activity. Identified conflicts of interest are mitigated by AKH prior to accreditation of the activity. AKH planners and reviewers have no relevant financial relationships to disclose.

Disclosure of Unlabeled Use and Investigational Product 
This educational activity may include discussion of uses of agents that are investigational and/or unapproved by the FDA. Please refer to the official prescribing information for each product for discussion of approved indications, contraindications, and warnings.

Disclaimer 
This course is designed solely to provide the healthcare professional with information to assist in his/her practice and professional development and is not to be considered a diagnostic tool to replace professional advice or treatment. The course serves as a general guide to the healthcare professional, and therefore, cannot be considered as giving legal, nursing, medical, or other professional advice in specific cases. AKH Inc. specifically disclaim responsibility for any adverse consequences resulting directly or indirectly from information in the course, for undetected error, or through participants misunderstanding of the content. If you would like to opt out from future communications from AKH please send an email to [email protected] with your information with "Opt Out" in the subject line.

Reviewer(s)

Dorothy Caputo, MA BSN RN

has no relevant financial relationships to disclose at this time.
Speaker, Instructor, Faculty(s)

Diana Bharucha-Goebel, Medical Director, Gene Therapy Center of Excellence, Nationwide Children's Hospital

has no relevant financial relationships to disclose at this time.

Urvi Desai

has a financial relationship (Advisor) with Alexion;.
has a financial relationship (Advisor) with Amgen;.
has a financial relationship (Advisor) with Argenx;.
has a financial relationship (Advisor) with Astra Zanaca;.

Eleni Drakou, MD

has no relevant financial relationships to disclose at this time.

Kevin Flanigan

has a financial relationship (Consultant) with Solid;.
has a financial relationship (Consultant) with Avidity;.
has a financial relationship (Consultant) with Dyne;.

Chet Villa

has no relevant financial relationships to disclose at this time.

Michele Yang, Associate Professor, Department of Neurology and Pediatrics

has a financial relationship (Advisor) with PTC Therapeutics;.
has a financial relationship (Advisor) with sarepta ;.
has a financial relationship (Speaker) with ScholarRock;.
has a financial relationship (Advisor) with Regenxbio;.

In support of improving patient care, this activity has been planned and implemented by AKH Inc., Advancing Knowledge in Healthcare and Muscular Dystrophy Association. AKH Inc., Advancing Knowledge in Healthcare is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.

 

This activity was planned by and for the healthcare team, and learners will receive 1 Interprofessional Continuing Education (IPCE) credit for learning and change.

 

Physicians
AKH Inc., Advancing Knowledge in Healthcare designates this live activity for a maximum of 1 AMA PRA Category 1 Credit(s)™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.

Pharmacists
AKH Inc., Advancing Knowledge in Healthcare designates this continuing education activity for 1 contact hours.

Nursing
Credit being awarded: 1 ANCC contact hours

Physician Associates
AKH Inc., Advancing Knowledge in Healthcare has been authorized by the American Academy of Physician Associates (AAPA) to award AAPA Category 1 CME credit for activities planned in accordance with AAPA CME Criteria. This activity is designated for 1 AAPA Category 1 CME credits. PAs should only claim credit commensurate with the extent of their participation.

 

Nurse Practitioners
This activity has been planned and implemented in accordance with the Accreditation Standards of the American Association of Nurse Practitioners (AANP) through the joint providership of AKH Inc., Advancing Knowledge in Healthcare and Muscular Dystrophy Association.  AKH Inc., Advancing Knowledge in Healthcare is accredited by the American Association of Nurse Practitioners as an approved provider of nurse practitioner continuing education. Provider number: 030803. This activity is approved for 1 contact hour(s) (which includes 0 hour(s) of pharmacology).

Social Workers
As a Jointly Accredited Organization, AKH Inc., Advancing Knowledge in Healthcare is approved to offer social work continuing education by the Association of Social Work Boards (ASWB) Approved Continuing Education (ACE) program. Organizations, not individual courses, are approved under this program. State and provincial regulatory boards have the final authority to determine whether an individual course may be accepted for continuing education credit. AKH Inc. Advancing Knowledge in Healthcare maintains responsibility for this course. Social workers completing this course receive 1 type continuing education credits.

 

Available Credit

  • 1.00 AANP
  • 1.00 AAPA Category 1 CME
  • 1.00 ACPE Pharmacist
  • 1.00 AMA PRA Category 1 Credit™
  • 1.00 ANCC
  • 1.00 ASWB
  • 1.00 Attendance

Price

Cost:
$0.00
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